Nucleic Acid Agents For Use In Treating Facioscapulohumeral Dystrophy (Fshd) - EP3192880

The patent EP3192880 was granted to Fred Hutchinson Cancer Research Center on Oct 9, 2019. The application was originally filed on Aug 18, 2011 under application number EP16191567A. The patent is currently recorded with a legal status of "Revoked".

EP3192880

FRED HUTCHINSON CANCER RESEARCH CENTER
Application Number
EP16191567A
Filing Date
Aug 18, 2011
Status
Revoked
May 20, 2022
Grant Date
Oct 9, 2019
External Links
Slate, Register, Google Patents

Patent Summary

Patent Family

Patent Family

Patent Oppositions (2)

Patent oppositions filed by competitors challenge the validity of a granted patent. These oppositions are typically based on claims of prior art, lack of novelty, or non-obviousness. They are a key part of the process for determining a patent's strength and enforceability.

CompanyOpposition DateRepresentativeOpposition Status

Get instant alerts for new oppositions and patent status changes

STRAWMANJul 8, 2020MEWBURN ELLISADMISSIBLE
REDDIE & GROSEJul 7, 2020CARRIDGEADMISSIBLE

Patent Citations (9) New

Patent citations refer to prior patents cited during different phases such as opposition or international search.

Citation PhasePublication NumberPublication Link
DESCRIPTIONFR2422956
DESCRIPTIONUS4376110
OPPOSITIONEP2426203
OPPOSITIONWO2013016352
SEARCHEP2426203
SEARCHUS2009280517
SEARCHWO2005037231
SEARCHWO2013016352
SEARCHWO2013019623

Non-Patent Literature (NPL) Citations (132) New

NPL citations refer to non-patent references such as research papers, articles, or other publications cited during examination or opposition phases.

Citation PhaseReference TextLink
DESCRIPTION- ALLO ET AL., NAT STRUCT MOL BIOL, (2009), vol. 16, pages 717 - 724-
DESCRIPTION- ALTSCHUL ET AL., NUCLEIC ACIDS RESEARCH, (1997), vol. 25, pages 3389 - 3402-
DESCRIPTION- AUSUBEL ET AL., Current Protocols in Molecular Biology, CURRENT PROTOCOLS PUBLISHING, (1994), vol. 2-
DESCRIPTION- BELANCIO ET AL., SEMIN. CANCER BIOL, (2010), vol. 20, pages 200 - 210-
DESCRIPTION- BOOTH ET AL., GENE, (2007), vol. 387, pages 7 - 14-
DESCRIPTION- BOOTH; HOLLAND, GENE, (2007), vol. 387, pages 7 - 14-
DESCRIPTION- BOSNAKOVSKI D. ET AL., PLOS ONE, (2009), vol. 4, page E7003-
DESCRIPTION- BOSNAKOVSKI ET AL., EXP NEUROL, (2008), vol. 214, no. 1, pages 87 - 96-
DESCRIPTION- BOSNAKOVSKI ET AL., PLOS ONE, (2009), vol. 4, page E7003-
DESCRIPTION- CAO ET AL., DEV. CELL, (2010), vol. 18, pages 662 - 674-
DESCRIPTION- CHANG ET AL., PLOS ONE, (2011), vol. 6, page E16867-
DESCRIPTION- CLAPP ET AL., AM J HUM GENET, (2007), vol. 57, pages 264 - 279-
DESCRIPTION- CLAPP ET AL., AM. J. HUM. GENET, (2007), vol. 57, pages 264 - 279-
DESCRIPTION- CLAPP ET AL., AM J HUM GENET, (2007), vol. 81, pages 264 - 279-
DESCRIPTION- CLAPP ET AL., AM. J. HUM. GENET, (2007), vol. 81, pages 264 - 279-
DESCRIPTION- D. BOSNAKOVSKI ET AL., EMBO J., (2008), vol. 27, pages 2766 - 2779-
DESCRIPTION- DE GREEF ET AL., HUM MUTAT, (2009), vol. 30, pages 1449 - 1459-
DESCRIPTION- DE GREEF ET AL., HUM. MUTAT., (2009), vol. 30, pages 1449 - 1459-
DESCRIPTION- D. GABELLINI ET AL., CELL, (2002), vol. 110, pages 339 - 348-
DESCRIPTION- DIXIT ET AL., PNAS, (2007), vol. 104, pages 18157 - 18162-
DESCRIPTION- DU ET AL., BIOINFORMATICS, (2008), vol. 24, pages 1547 - 1548-
DESCRIPTION- E. BEAUDOING ET AL., GENOME RES, (2000), vol. 10, pages 1001 - 1010-
DESCRIPTION- EUR. J. IMMUNOL., (1976), vol. 6, page 292-
DESCRIPTION- EUR. J. IMMUNOL., (1976), vol. 6, page 511-
DESCRIPTION- F. AHMED ET AL., IN SILICO BIOL, (2009), vol. 9, pages 135 - 148-
DESCRIPTION- FALCON; GENTLEMAN, BIOINFORMATICS, (2007), vol. 23, pages 257 - 258-
DESCRIPTION- FRISULLO ET AL., J. CLIN. IMMUNOL., (2011), vol. 31, pages 155 - 166-
DESCRIPTION- GABELLINI ET AL., CELL, (2002), vol. 110, pages 339 - 348-
DESCRIPTION- GABELLINI ET AL., NATURE, (2006), vol. 439, pages 973 - 977-
DESCRIPTION- GABRIELS ET AL., GENE, (1999), vol. 236, pages 25 - 32-
DESCRIPTION- GENG ET AL., HYBRIDOMA, (2011), vol. 30, no. 2, pages 125 - 30-
DESCRIPTION- GENG ET AL., HYBRIDOMA (LARCHMT, (2011), vol. 30, pages 125 - 130-
DESCRIPTION- GENG ET AL., LARCHMT, (2011), vol. 30, pages 125 - 130-
DESCRIPTION- H. LIU ET AL., BIOINFORMATICS, (2005), vol. 21, pages 671 - 673-
DESCRIPTION- HOLLAND ET AL., BMC BIOL., (2007), vol. 5, page 47-
DESCRIPTION- J.C. DE GREEF ET AL., HUM MUTAT, (2009), vol. 30, pages 1449 - 1459-
DESCRIPTION- J.C. DE GREEF ET AL., MUTAT RES, (2008), vol. 647, pages 94 - 102-
DESCRIPTION- J.C. VAN DEUTEKOM ET AL., HUM MOL GENET, (1993), vol. 2, pages 2037 - 2042-
DESCRIPTION- J.C. VAN DEUTKOM ET AL., HUM MOL GENET, (1993), vol. 2, pages 2037 - 2042-
DESCRIPTION- JENSEN, J. ET AL., NAT. GENET., (1999), vol. 21, pages 209 - 12-
DESCRIPTION- JI Z ET AL., PLOS ONE, (2009), vol. 4, page E8419-
DESCRIPTION- KAESSMANN H. ET AL., NAT REV GENET, (2009), vol. 10, pages 19 - 31-
DESCRIPTION- KAWAMURA-SAITO ET AL., HUM. MOL. GENET, (2006), vol. 15, pages 2125 - 2137-
DESCRIPTION- KLOOSTER ET AL., EUR. J. HUM. GENET., (2009), vol. 17, pages 1615 - 1624-
DESCRIPTION- KNOEPFLER ET AL., NUCLEIC ACIDS RES, (1999), vol. 27, pages 3752 - 3761-
DESCRIPTION- KOWALJOW ET AL., NEURAMUSCUL. DISORD, (2007), vol. 17, pages 611 - 623-
DESCRIPTION- KOWALJOW ET AL., NEUROMUSCUL. DISCORD, (2007), vol. 17, pages 611 - 623-
DESCRIPTION- KOWALJOW ET AL., NEUROMUSCUL DISORD, (2007), vol. 17, pages 611 - 623-
DESCRIPTION- LAOUDJ-CHENIVESSE ET AL., J. MOL. MED., (2005), vol. 83, pages 216 - 224-
DESCRIPTION- LEMMER ET AL., AM J HUM GENET, (2007), vol. 81, pages 884 - 894-
DESCRIPTION- LEMMERS ET AL., AM J. HUM GENET, (2004), vol. 75, pages 1124 - 1130-
DESCRIPTION- LEMMERS ET AL., AM J HUM GENET, (2007), vol. 57, pages 884 - 894-
DESCRIPTION- LEMMERS ET AL., AM J. HUM GENET, (2007), vol. 81, pages 884 - 894-
DESCRIPTION- LEMMERS ET AL., AM J. HUM GENET, (2010), vol. 86, pages 364 - 377-
DESCRIPTION- LEMMERS ET AL., HUM MOL GENET, (1998), vol. 7, pages 1207 - 1214-
DESCRIPTION- LEMMERS ET AL., NAT GENET, (2002), vol. 32, pages 235 - 236-
DESCRIPTION- LEMMERS ET AL., SCIENCE, (2010), vol. 329, no. 5999, pages 1 650 - 3-
DESCRIPTION- LEMMERS ET AL., SCIENCE, (2010), vol. 329, pages 1650 - 1653-
DESCRIPTION- L. SNIDER ET AL., HUM MOL GENET, (2009), vol. 18, pages 2414 - 2430-
DESCRIPTION- LUCO ET AL., SCIENCE-
DESCRIPTION- LUCO ET AL., SCIENCE, (2010), vol. 327, no. 5968, pages 996 - 1000-
DESCRIPTION- LYLE ET AL., GENOMICS, (1995), vol. 25, pages 389 - 397-
DESCRIPTION- M. DIXIT ET AL., PNAS, (2007), vol. 104, pages 18157 - 18162-
DESCRIPTION- MOLNAR ET AL., EUR. ARCH. PSYCHIATRY CLIN. NEUROSCIE, (1991), vol. 241, pages 105 - 108-
DESCRIPTION- Monoclonal Antibodies and T-Cell Hybridomas, ELSEVIER, (1981), pages 563 - 681-
DESCRIPTION- NATURE, (1975), vol. 256, page 495-
DESCRIPTION- NELSON ET AL., NAT PROTOC, (2006), vol. 1, pages 179 - 185-
DESCRIPTION- PALII ET AL., EMBO J., (2011), vol. 30, pages 494 - 509-
DESCRIPTION- PARKER H ET AL., SCIENCE, (2009), vol. 325, pages 995 - 998-
DESCRIPTION- PFAFFL, NUCLEIC ACIDS RES, (2001), vol. 29, page E45-
DESCRIPTION- P.G. VAN OVERVELD ET AL., NAT GENET, (2003), vol. 35, pages 315 - 317-
DESCRIPTION- P.S. MASNY ET AL., EUR J. HUM GENET, (2010), vol. 75, pages 448 - 456-
DESCRIPTION- REED ET AL., EXP. NEURAL., (2007), vol. 205, pages 583 - 586-
DESCRIPTION- R.J. LEMMERS ET AL., AM J. HUM GENET, (2007), vol. 81, pages 884 - 894-
DESCRIPTION- R.J. LEMMERS ET AL., AM J. HUM GENET, (2010), vol. 86, pages 364 - 377-
DESCRIPTION- R. J. LEMMERS ET AL., HUM. MOL. GENET., (1998), vol. 7, pages 1207 - 1214-
DESCRIPTION- R. KLOOSTER ET AL., EUR J. HUM GENET, (2009), vol. 17, pages 1615 - 1624-
DESCRIPTION- R. KLOOSTER ET AL., EUR. J. HUM GENET, (2009), vol. 17, pages 1615 - 1624-
DESCRIPTION- R. TAWIL ET AL., MUSCLE NERVE, (2006), vol. 34, pages 1 - 15-
DESCRIPTION- R. TUPLER ET AL., J MED GENET, (1996), vol. 33, pages 366 - 370-
DESCRIPTION- SAMBROOK ET AL., Molecular Cloning: A Laboratory Manual, COLD SPRING HARBOR LABORATORY, (1989), vol. 1-3-
DESCRIPTION- SANGER ET AL., PNAS (USA), (1977), vol. 74, no. 12, pages 5463 - 5467-
DESCRIPTION- SCHULZ ET AL., J. BIOMED. BIOTECHNOL., (2006), page 83672-
DESCRIPTION- SIMPSON ET AL., NAT. REV. CANCER, (2005), vol. 5, pages 615 - 625-
DESCRIPTION- S.M. VAN DER MAAREL ET AL., AM J HUM GENET, (2000), vol. 66, pages 26 - 35-
DESCRIPTION- SNIDER ET AL., HUM MOL GENET, (2009), vol. 18, pages 2414 - 2430-
DESCRIPTION- SNIDER ET AL., HUM MOL GENET, (2009), vol. 75, pages 2414 - 2430-
DESCRIPTION- SNIDER ET AL., PLOS GENET, (2010), vol. 6, page E1001181-
DESCRIPTION- TAKAHASHI ET AL., CELL, (2007), vol. 131, pages 861 - 872-
DESCRIPTION- TAM ET AL., NATURE, (2008), vol. 453, pages 543 - 538-
DESCRIPTION- TATIANA, A. ET AL., "Blast 2 Sequences A New Tool for Comparing Protein and Nucleotide Sequences", FEMS MICROBIOL. LETT., (1999), vol. 174, pages 247 - 250-
DESCRIPTION- TAWIL, R. ET AL., MUSCLE NERVE, (2006), vol. 34, pages 1 - 15-
DESCRIPTION- TUPLET ET AL., J. MED. GENET., (1996), vol. 33, pages 366 - 370-
DESCRIPTION- VAN OVERVELD ET AL., NAT GENET, (2003), vol. 35, pages 315 - 317-
DESCRIPTION- VAN OVERVELD ET AL., NAT. GENET., (2003), vol. 35, pages 315 - 317-
DESCRIPTION- WALLACE ET AL., ANN. NEURAL, (2011), vol. 69, pages 540 - 552-
DESCRIPTION- WALLACE ET AL., ANN REV. NEUROL., (2011), vol. 69, no. 3, pages 540 - 52-
DESCRIPTION- WATANABE ET AL., NATURE, (2008), vol. 453, pages 539 - 543-
DESCRIPTION- WETTENHALL; SMYTH, BIOINFORMATICS, (2004), vol. 20, pages 3705 - 3706-
DESCRIPTION- WIJMENGA ET AL., NAT GENET, (1992), vol. 2, pages 26 - 30-
DESCRIPTION- WIJMENGA ET AL., NAT. GENET, (1992), vol. 2, pages 26 - 30-
DESCRIPTION- WOOTTON, J.C.; S. FEDERHEN, METHODS IN ENZYMOLOGY, (1996), vol. 266, pages 554 - 571-
DESCRIPTION- WUEBBLES ET AL., INT. J. CLIN. EXP. PATHOL., (2010), vol. 3, pages 386 - 400-
DESCRIPTION- WU ET AL., DUXBL DEV. DYN, (2010), vol. 239, pages 927 - 940-
DESCRIPTION- WU ET AL., DUXBL DEV DYN, vol. 239, pages 927 - 940-
DESCRIPTION- WU S.L. ET AL., DUXBL DEV DYN, (2010), vol. 239, pages 927 - 940-
DESCRIPTION- W. ZENG ET AL., PLOS GENET, (2009), vol. 5, page E1000559-
DESCRIPTION- W. ZENG ET AL., PLOS GENET, (2009), vol. 5, page EI0000559-
DESCRIPTION- ZENG ET AL., PLOS GENET, (2009), vol. 5, page E 1000559-
DESCRIPTION- ZENG ET AL., PLOS GENET, (2009), vol. 5, page E1000559-
DESCRIPTION- ZENG ET AL., PLOS GENET, (2009), vol. 5, page EI000559-
DESCRIPTION- ZENG, W. ET AL., PLOS GENET, (2009), vol. 5, page EI000559-
OPPOSITION- JOEL CHAMBERLAIN, "Validity of RNAi-based therapeutics as a treatment for FSHD as demonstrated in a mouse model of muscular dystrophy", MDA National Scientific Conference - Neuromuscular Therapeutic Strategies: Overcoming the Barriers from Microscope to Marketplace (Book of Abstracts, (20110313), page 40, XP055766732-
OPPOSITION- C Vanderplanck et al, "KEYNOTE 5: SUPPRESSION OF DUX4 OR DUX4C EXPRESSION BY ANTISENSE STRATEGIES IN A THERAPEUTIC APPROACH FOR FSHD", 7th Australasian Gene Theraphy Society Meeting, The Journal of Gene Medicine, vol. 13, no. 7-8, doi:10.1002/jgm, page 414, XP055214328
OPPOSITION- VANDERPLANK et al., "Keynote 5: Suppression of DUX4 or DUX4C expression by antisense strategies in a therapeutic approach for FSHD", 7th Australasian Gene Therapy Society Meeting , Journal of Gene Medicine, (20110627), vol. 13, no. 7-8, pages 410 - 446, XP055162336
OPPOSITION- Silvre M. van der Maarel; Rabi Tawil; Stephen J. Tapscott;, "Facioscapulohumeral muscular dystrophy and DUX4: breaking the silence", Trends in Molecular Medicine, Elsevier Current Trends, GB, GB, vol. 17, no. 5, doi:10.1016/j.molmed.2011.01.001, ISSN 1471-4914, pages 252 - 258, XP028206228
OPPOSITION- Lindsay M Wallace et al, "Developing RNAi Therapy for FSHD", Molecular Therapy, No longer published by Elsevier, (20090501), vol. 17, no. Suppl. 1, doi:10.1038.mt.2009.106, ISSN 1525-0016, page S151, XP055162326
OPPOSITION- BORTOLANZA et al., "AAV6-mediated Systemic shRNA Delivery Reverses Disease in a Mouse Model of Facioscapulohumeral Muscular Dystrophy", Molecular Therapy, vol. 19, no. 11, doi:10.1038/mt.2011.153, (20110809), pages 2055 - 2064, XP055656938
OPPOSITION- Jenny K W Lam et al, "siRNA Versus miRNA as Therapeutics for Gene Silencing", Molecular Therapy: Nucleic Acids., Cell Press, US, US, (20150101), vol. 4, doi:10.1038/mtna.2015.23, ISSN 2162-2531, pages 1 - 20, XP055380675
OPPOSITION- L. Snider et al, "RNA transcripts, miRNA-sized fragments and proteins produced from D4Z4 units: new candidates for the pathophysiology of facioscapulohumeral dystrophy", Human Molecular Genetics, (20090701), vol. 18, no. 13, doi:10.1093/hmg/ddp180, ISSN 09646906, pages 2414 - 2430, XP055091920
OPPOSITION- SNIDER et al., "RNA transcripts, miRNA-sized fragments and proteins produced from D4Z4 units: new candidates for the pathophysiology of facioscapulohumeral dystrophy", Human Molecular Genetics, (20090000), vol. 18, no. 13, doi:10.1093/hmg/ddp180, pages 2414 - 2430, XP055091920
OPPOSITION- R. J. L. F. Lemmers et al, "A Unifying Genetic Model for Facioscapulohumeral Muscular Dystrophy", Science, American Association for the Advancement of Science, (20100924), vol. 329, no. 5999, doi:10.1126/science.1189044, ISSN 00368075, pages 1650 - 1653, XP055091773
OPPOSITION- C. Frank Bennett, Eric E. Swayze, "RNA Targeting Therapeutics: Molecular Mechanisms of Antisense Oligonucleotides as a Therapeutic Platform", Annual Review of Pharmacology and Toxicology, Annual Reviews Inc., (20100201), vol. 50, no. 1, doi:10.1146/annurev.pharmtox.010909.105654, ISSN 03621642, pages 259 - 293, XP055055378
OPPOSITION- Lauren Snide et al, "Facioscapulohumeral Dystrophy: Incomplete Suppression of a Retrotransposed Gene", PLoS Genetics, Public Library of Science, (20100101), vol. 6, no. 10, doi:10.1371/journal.pgen.1001181, ISSN 15537390, page e1001181, XP055011341
OPPOSITION- SNIDER et al., "Facioscapulohumeral Dystrophy: Incomplete Suppression of a Retrotransposed Gene", PLOS Genetics, (20101028), vol. 6, no. 10, doi:10.1371/journal.pgen.1001181, XP055011341
OPPOSITION- Eugenie Ansseau et al, "DUX4c Is Up-Regulated in FSHD. It Induces the MYF5 Protein and Human Myoblast Proliferation", PLoS ONE, Public Library of Science, (20090101), vol. 4, no. 10, doi:10.1371/journal.pone.0007482, ISSN 19326203, page e7482, XP055011327
SEARCH- "Human double homeobox 4 (DUX4) mRNA SEQ ID NO:46.", Geneseq, (20120412), Database accession no. AZT86869, URL: EBI, XP002717599 [P] * sequence . *-
SEARCH[XPYI] - VANDERPLANCK C ET AL, "Keynote 5: Suppression of DUX4 or DUX4C expression by antisense strategies in a therapeutic approach for FSHD", JOURNAL OF GENE MEDICINE, US, (20110701), vol. 13, no. 7-8, doi:10.1002/jgm.1582, ISSN 1099-498X, page 414, XP055162336 [XP] 1-4,7 * the whole document * [Y] 1-8 [I] 5,6,8
SEARCH- DIXIT M. ET AL, "DUX4, a candidate gene of facioscapulohumeral muscular dystrophy, encodes a transcriptional activator of PITX1", PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES, (20071107), vol. 104, no. 46, doi:10.1073/pnas.0708659104, ISSN 0027-8424, pages 18157 - 18162, XP055075929 [AD] 1-8 * abstract * * page 18160, column 2, paragraph 3 - page 18161, column 1, paragraph 4 *
SEARCH- SNIDER L ET AL, "RNA transcripts, miRNA-sized fragments and proteins produced from D4Z4 units: new candidates for the pathophysiology of facioscapulohumeral dystrophy", HUMAN MOLECULAR GENETICS, (20090409), vol. 18, no. 13, doi:10.1093/hmg/ddp180, ISSN 0964-6906, pages 2414 - 2430, XP055091920 [A] 1-8 * abstract * * page 2421, column 1, paragraph 2 - column 2, paragraph 1 * * page 2423, column 1, paragraph 2 - page 2424, column 1, paragraph 1 *
SEARCH- LEMMERS R J L F ET AL, "A unifying genetic model for facioscapulohumeral muscular dystrophy", SCIENCE, (20100924), vol. 329, no. 5999, doi:10.1126/science.1189044, ISSN 0036-8075, pages 1650 - 1653, XP055091773 [YP] 1-8 * the whole document *
SEARCH- SNIDER L ET AL, "Facioscapulohumeral Dystrophy: Incomplete Suppression of a Retrotransposed Gene", PLOS GENETICS, (20101028), vol. 6, no. 10, doi:10.1371/journal.pgen.1001181, ISSN 1553-7390, page e1001181, XP055011341 [YP] 1-8 * the whole document *

Download Citation Report

Get a free citation report including examiner, opposition, and international search citations.

Get Citation Report

Dossier Documents

The dossier documents provide a comprehensive record of the patent’s prosecution history - including filings, correspondence, and decisions made by patent offices - and are crucial for understanding the patent’s legal journey and any challenges it may have faced during examination.

  • Date

    Description

  • Get instant alerts for new documents