Methods And Compositions For The Treatment Of Monogenic Diseases - EP3196301

The patent EP3196301 was granted to Sangamo Biosciences on Oct 17, 2018. The application was originally filed on Mar 15, 2013 under application number EP16198961A. The patent is currently recorded with a legal status of "Revoked".

EP3196301

SANGAMO BIOSCIENCES
Application Number
EP16198961A
Filing Date
Mar 15, 2013
Status
Revoked
Jul 3, 2020
Publication Date
Oct 17, 2018
External Links
Slate, Register, Google Patents

Patent Summary

Patent Family

Patent Family

Patent Oppositions (3)

Patent oppositions filed by competitors challenge the validity of a granted patent. These oppositions are typically based on claims of prior art, lack of novelty, or non-obviousness. They are a key part of the process for determining a patent's strength and enforceability.

CompanyOpposition DateRepresentativeOpposition Status

Get instant alerts for new oppositions and patent status changes

LEEMINGJul 17, 2019J A KEMPADMISSIBLE
MATHYS & SQUIREJul 17, 2019FORDADMISSIBLE
PATENT BOUTIQUEJul 15, 2019-ADMISSIBLE

Patent Citations (90) New

Patent citations refer to prior patents cited during different phases such as opposition or international search.

Citation PhasePublication Number
DESCRIPTIONWO1994US05700
DESCRIPTIONGB2338237
DESCRIPTIONUS2003232410
DESCRIPTIONUS2005026157
DESCRIPTIONUS2005208489
DESCRIPTIONUS2006063231
DESCRIPTIONUS2006188987
DESCRIPTIONUS2007117128
DESCRIPTIONUS2008159996
DESCRIPTIONUS2008299580
DESCRIPTIONUS2009054985
DESCRIPTIONUS2009068164
DESCRIPTIONUS2010218264
DESCRIPTIONUS2011301073
DESCRIPTIONUS2013137104
DESCRIPTIONUS4186183
DESCRIPTIONUS4217344
DESCRIPTIONUS4235871
DESCRIPTIONUS4261975
DESCRIPTIONUS4485054
DESCRIPTIONUS4501728
DESCRIPTIONUS4774085
DESCRIPTIONUS4797368
DESCRIPTIONUS4837028
DESCRIPTIONUS4897355
DESCRIPTIONUS4946787
DESCRIPTIONUS5049386
DESCRIPTIONUS5173414
DESCRIPTIONUS5176996
DESCRIPTIONUS5356802
DESCRIPTIONUS5420032
DESCRIPTIONUS5422251
DESCRIPTIONUS5436150
DESCRIPTIONUS5487994
DESCRIPTIONUS5585245
DESCRIPTIONUS5789538
DESCRIPTIONUS5925523
DESCRIPTIONUS6007988
DESCRIPTIONUS6008336
DESCRIPTIONUS6013453
DESCRIPTIONUS6140081
DESCRIPTIONUS6140466
DESCRIPTIONUS6200759
DESCRIPTIONUS6242568
DESCRIPTIONUS6410248
DESCRIPTIONUS6453242
DESCRIPTIONUS6479626
DESCRIPTIONUS6534261
DESCRIPTIONUS6723551
DESCRIPTIONUS6833252
DESCRIPTIONUS6903185
DESCRIPTIONUS7153949
DESCRIPTIONUS7888121
DESCRIPTIONWO0027878
DESCRIPTIONWO0160970
DESCRIPTIONWO0188197
DESCRIPTIONWO02077227
DESCRIPTIONWO02099084
DESCRIPTIONWO0216536
DESCRIPTIONWO03016496
DESCRIPTIONWO2007014275
DESCRIPTIONWO2009042163
DESCRIPTIONWO2009068164
DESCRIPTIONWO2010079430
DESCRIPTIONWO9116024
DESCRIPTIONWO9117424
DESCRIPTIONWO9324641
DESCRIPTIONWO9519431
DESCRIPTIONWO9606166
DESCRIPTIONWO9837186
DESCRIPTIONWO9844350
DESCRIPTIONWO9853057
DESCRIPTIONWO9853058
DESCRIPTIONWO9853059
DESCRIPTIONWO9853060
DESCRIPTIONWO9854311
OPPOSITIONWO2010117464
OPPOSITIONWO2011011767
OPPOSITIONWO2011097036
OPPOSITIONWO2011100058
OPPOSITIONWO2012015938
OPPOSITIONWO2013044008
OPPOSITIONWO2013063315
OPPOSITIONWO2013158309
OPPOSITIONWO2014011237
SEARCHWO2010117464
SEARCHWO2011011767
SEARCHWO2011097036
SEARCHWO2011100058
SEARCHWO2012015938

Non-Patent Literature (NPL) Citations (129) New

NPL citations refer to non-patent references such as research papers, articles, or other publications cited during examination or opposition phases.

Citation PhaseReference Text
DESCRIPTION- AHMAD ET AL., CANCER RES., (1992), vol. 52, pages 4817 - 4820
DESCRIPTION- ALVAREZ ET AL., HUM. GENE THER., (1997), vol. 5, pages 597 - 613
DESCRIPTION- ANDERSON, SCIENCE, (1992), vol. 256, pages 808 - 813
DESCRIPTION- ARGAST ET AL., J. MOL. BIOL., (1998), vol. 280, pages 345 - 353
DESCRIPTION- ASHWORTH ET AL., NATURE, (2006), vol. 441, pages 656 - 659
DESCRIPTION- AYUSO ET AL., GENE THER, (2010), vol. 17, no. 4, pages 503 - 510
DESCRIPTION- BEERLI ET AL., NATURE BIOTECHNOL., (2002), vol. 20, pages 135 - 141
DESCRIPTION- BEHR ET AL., BIOCONJUGATE CHEM., (1994), vol. 5, pages 382 - 389
DESCRIPTION- BELFORT ET AL., NUCLEIC ACIDS RES., (1997), vol. 25, pages 3379 - 3388
DESCRIPTION- BITINAITE ET AL., PROC. NATL. ACAD. SCI. USA, (1998), vol. 95, pages 10570 - 10575
DESCRIPTION- BLAESE ET AL., CANCER GENE THER., (1995), vol. 2, pages 291 - 297
DESCRIPTION- BLAESE ET AL., SCIENCE, (1995), vol. 270, pages 475 - 480
DESCRIPTION- BOCH ET AL., SCIENCE, (2009), vol. 326, pages 1509 - 1512
DESCRIPTION- BONAS ET AL., MOL GEN GENET, (1989), vol. 218, pages 127 - 136
DESCRIPTION- BUCHSCHER ET AL., J. VIROL., (1992), vol. 66, pages 2731 - 2739
DESCRIPTION- CHANG ET AL., PROC. NATL. ACAD. SCI. USA, (1987), vol. 84, pages 4959 - 4963
DESCRIPTION- CHEVALIER ET AL., MOLEC. CELL, (2002), vol. 10, pages 895 - 905
DESCRIPTION- CHOO ET AL., CURR. OPIN. STRUCT. BIOL., (2000), vol. 10, pages 411 - 416
DESCRIPTION- "Chromatin", METHODS IN ENZYMOLOGY, ACADEMIC PRESS, (1999), vol. 304
DESCRIPTION- "Chromatin Protocols", METHODS IN MOLECULAR BIOLOGY, HUMANA PRESS, (1999), vol. 119
DESCRIPTION- CRYSTAL, SCIENCE, (1995), vol. 270, pages 404 - 410
DESCRIPTION- DAVID SEGAL, ELIFE, (2013), vol. 2, page E00563
DESCRIPTION- DILLON, TIBTECH, (1993), vol. 11, pages 167 - 175
DESCRIPTION- DRANOFF ET AL., HUM. GENE THER., (1997), vol. 1, pages 111 - 112
DESCRIPTION- DUJON ET AL., GENE, (1989), vol. 82, pages 115 - 118
DESCRIPTION- DULL ET AL., J. VIROL., (1998), vol. 72, pages 8463 - 8471
DESCRIPTION- DUNBAR ET AL., BLOOD, (19950601), vol. 85, no. 11, pages 3048 - 3057
DESCRIPTION- ELLEM ET AL., IMMUNOL IMMUNOTHER., (1997), vol. 44, no. 1, pages 10 - 20
DESCRIPTION- EPINAT ET AL., NUCLEIC ACIDS RES., (2003), vol. 31, pages 2952 - 2962
DESCRIPTION- FIELDS ET AL., NATURE, (1989), vol. 340, pages 245 - 246
DESCRIPTION- FOLLENZI ET AL., NATURE GENETICS, (2000), vol. 25, pages 217 - 222
DESCRIPTION- GABATHULER ET AL., NEUROBIOLOGY OF DISEASE, (2010), vol. 37, pages 48 - 57
DESCRIPTION- GAO ET AL., GENE THERAPY, (1995), vol. 2, pages 710 - 722
DESCRIPTION- GIMBLE ET AL., J. MOL. BIOL., (1996), vol. 263, pages 163 - 180
DESCRIPTION- GUSCHIN ET AL., METHODS MOL BIOL., (2010), vol. 649, pages 247 - 256
DESCRIPTION- HAN ET AL., PROC. NATL. ACAD. SCI. USA, (1995), vol. 92, pages 9747 - 9751
DESCRIPTION- HERMONAT; MUZYCZKA, PNAS, (1984), vol. 81, pages 6466 - 6470
DESCRIPTION- HEUER ET AL., APPL ANDENVIR MICRO, (2007), vol. 73, no. 13, pages 4379 - 4384
DESCRIPTION- HEUER ET AL., APPLIED AND ENVIRONMENTAL MICROBIOLOGY, (2007), vol. 73, no. 13, pages 4379 - 4384
DESCRIPTION- ISALAN ET AL., NATURE BIOTECHNOL., (2001), vol. 19, pages 656 - 660
DESCRIPTION- JASIN, TRENDS GENET., (1996), vol. 12, pages 224 - 228
DESCRIPTION- JINEK ET AL., ELIFE, (2013), vol. 2, page E00471
DESCRIPTION- JINEK ET AL., SCIENCE, (2012), vol. 337, pages 816 - 821
DESCRIPTION- JOHANN ET AL., J. VIROL., (1992), vol. 66, pages 1635 - 1640
DESCRIPTION- KATHERINE PONDER, J CLIN INVEST, (2008), vol. 118, no. 8, page 2686
DESCRIPTION- KAY ET AL., SCIENCE, (2007), vol. 318, pages 648 - 651
DESCRIPTION- KEARNS ET AL., GENE THER., (1996), vol. 9, pages 748 - 755
DESCRIPTION- KIM ET AL., J. BIOL. CHEM., (199412), vol. 269, no. 50, pages 31978 - 31982
DESCRIPTION- KIM ET AL., PROC. NATL. ACAD. SCI. USA, (1994), vol. 91, pages 883 - 887
DESCRIPTION- KIM ET AL., PROC NAT'L ACAD SCI USA, (1996), vol. 93, no. 3, pages 1156 - 1160
DESCRIPTION- KOHN ET AL., NAT. MED., (199510), vol. 1, no. 10, pages 1017 - 1023
DESCRIPTION- KORMANN ET AL., NATURE BIOTECHNOLOGY, (2011), vol. 29, no. 2, pages 154 - 157
DESCRIPTION- KOTIN, HUMAN GENE THERAPY, (1994), vol. 5, pages 793 - 801
DESCRIPTION- KREMER; PERRICAUDET, BRITISH MEDICAL BULLETIN, (1995), vol. 51, no. 1, pages 31 - 44
DESCRIPTION- LI ET AL., NATURE, (2011), vol. 475, no. 7355, page 217
DESCRIPTION- LI ET AL., PROC. NATL. ACAD. SCI. USA, (1992), vol. 89, pages 4275 - 4279
DESCRIPTION- LI ET AL., PROC. NATL. ACAD. SCI. USA, (1993), vol. 90, pages 2764 - 2768
DESCRIPTION- MACDIARMID ET AL., NATURE BIOTECHNOLOGY, (2009), vol. 27, no. 7, page 643
DESCRIPTION- MALECH ET AL., PNAS, (1997), vol. 94, no. 22, pages 12133 - 12138
DESCRIPTION- METHODS IN ENZYMOLOGY, ACADEMIC PRESS
DESCRIPTION- MILLER ET AL., J. VIROL., (1991), vol. 65, pages 2220 - 2224
DESCRIPTION- MILLER, NATURE, (1992), vol. 357, pages 455 - 460
DESCRIPTION- MITANI; CASKEY, TIBTECH, (1993), vol. 11, pages 162 - 166
DESCRIPTION- MOSCOU; BOGDANOVE, SCIENCE, (2009), vol. 326, page 1501
DESCRIPTION- MUZYCZKA, J., CLIN. INVEST., (1994), vol. 94, page 1351
DESCRIPTION- NABEL; FELGNER, TIBTECH, (1993), vol. 11, pages 211 - 217
DESCRIPTION- NEHLS ET AL., SCIENCE, (1996), vol. 272, pages 886 - 889
DESCRIPTION- ORY ET AL., PROC. NATL. ACAD. SCI. USA, (1996), vol. 93, pages 11382 - 11388
DESCRIPTION- PABO ET AL., ANN. REV. BIOCHEM., (2001), vol. 70, pages 313 - 340
DESCRIPTION- PAQUES ET AL., CURRENT GENE THERAPY, (2007), vol. 7, pages 49 - 66
DESCRIPTION- PEREZ ET AL., NAT. BIOTECHNOL., (2008), vol. 26, pages 808 - 816
DESCRIPTION- PEREZ ET AL., NATURE BIOTECHNOLOGY, (2008), vol. 26, no. 7, pages 808 - 816
DESCRIPTION- PERLER ET AL., NUCLEIC ACIDS RES., (1994), vol. 22, pages 1125 - 1127
DESCRIPTION- REMY ET AL., BIOCONJUGATE CHEM., (1994), vol. 5, pages 647 - 654
DESCRIPTION- ROBERTS ET AL., NUCLEIC ACIDS RES., (2003), vol. 31, pages 418 - 420
DESCRIPTION- ROSENECKER ET AL., INFECTION, (1996), vol. 24, no. 1, pages 5 - 10
DESCRIPTION- SAMULSKI ET AL., J. VIROL., (198909), vol. 63, no. 9, pages 3822 - 3828
DESCRIPTION- SCHORNACK S ET AL., J PLANT PHYSIOL, (2006), vol. 163, no. 3, pages 256 - 272
DESCRIPTION- SEGAL ET AL., CURR. OPIN. BIOTECHNOL., (2001), vol. 12, pages 632 - 637
DESCRIPTION- SOMMERFELT ET AL., VIROL., (1990), vol. 176, pages 58 - 59
DESCRIPTION- STERMAN ET AL., HUM. GENE THER., (1998), vol. 7, pages 1083 - 1089
DESCRIPTION- STERMAN ET AL., HUM. GENE THER., (1998), vol. 9, no. 7, pages 1083 - 1089
DESCRIPTION- TOPF ET AL., GENE THER., (1998), vol. 5, pages 507 - 513
DESCRIPTION- TRATSCHIN ET AL., MOL. CELL. BIOL., (1984), vol. 4, pages 2072 - 2081
DESCRIPTION- TRATSCHIN ET AL., MOL. CELL. BIOL., (1985), vol. 5, pages 3251 - 3260
DESCRIPTION- URNOV ET AL., NATURE, (2005), vol. 435, no. 7042, pages 646 - 651
DESCRIPTION- VAN BRUNT, BIOTECHNOLOGY, (1988), vol. 6, no. 10, pages 1149 - 1154
DESCRIPTION- VIGNE, RESTORATIVE NEUROLOGY AND NEUROSCIENCE, (1995), vol. 8, pages 35 - 36
DESCRIPTION- WAGNER ET AL., LANCET, (1998), vol. 351, no. 9117, pages 1702 - 1703
DESCRIPTION- WELSH ET AL., HUM. GENE THER., (1995), vol. 2, pages 205 - 218
DESCRIPTION- WEST ET AL., VIROLOGY, (1987), vol. 160, pages 38 - 47
DESCRIPTION- WILSON ET AL., J. VIROL., (1989), vol. 63, pages 2374 - 2378
DESCRIPTION- YANG ET AL., BIOCHEMISTRY, (2000), vol. 39, pages 3533 - 3541
DESCRIPTION- YU ET AL., GENE THERAPY, (1994), vol. 1, pages 13 - 26
DESCRIPTION- ZUFFERY ET AL., J. VIROL., (1998), vol. 72, pages 9873 - 9880
OPPOSITION- ANGUELA et al., "751: In Vivo Genome Editing of Liver Albumin for Therapeutic Gene Expression: Rescue of Hemophilic Mice Via Integration of Factor 9", Blood; 54th Annual Meeting and Exposition of the American-Society-of-Hematology (ASH), (20121116), vol. 120, no. 21, page 751, XP009506560
OPPOSITION- ANGUELA et al., "In Vivo Genome Editing of Liver Albumin for Therapeutic Gene Expression: Rescue of Hemophilic Mice Via Integration of Factor 9", Blood, Abstracts et Meeting Program for the 54th ASH Annual Meeting, (20121208), page 1, XP002713765
OPPOSITION- ANGUELA X. M. et al., "abstract 751: In Vivo Genome Editing of Liver Albumin for Therapeutic Gene Expression: Rescue of Haemophilic November 2012 Mice Via Integration of Factor 9", Blood, vol. 120, no. 21, (20121116), URL: http://www.bloodjournal.org/content/120/21/751?sso-checked=true, XP055626923
OPPOSITION- BRUNI et al., "Update on Treatment of Lysosomal Storage Published July Diseases", Acta Mvologica, (20070100), vol. XXVI, pages 87 - 92, XP055077957
OPPOSITION- CHIAL H. et al, "Mendelian Genetics: Patterns of Inheritance and Published 2008 Single- Gene Disorders", Nature Education, (20080000), vol. 1, no. 1, page 63, XP055626874
OPPOSITION- "Choosing Targets for Gene Therapy", MATISSEK et al., Targets in Gene Therapy, InTech, (20110823), pages 3 - 28, ISBN 978-953-307-540-2, XP055626882
OPPOSITION- CONG et al., "Multiplex Genome Engineering Using CRISPR/Cas Systems", Science, (20130200), vol. 339, no. 6121, pages 819 - 823, XP002779503
OPPOSITION- "Danon disease", USA. gov, (20190625), pages 1 - 5, URL: https://ghr.nlm.nih.gov/condition/danon-disease, XP055626927
OPPOSITION- Dr. Tomislav Meštrović, "Single Gene Genetic Disorder", News Medical, (20180823), URL: https://www.news-medical.net/health/Single-Gene-Genetic-Disorder.aspx, XP055626885
OPPOSITION- SHARMA et al., "57. Correction of Hemophilia B Phenotype Following ZFN Mediated Genome Editing in Adult Mice", Molecular Therapy, (20120000), vol. 20, no. S1, page S24, XP055626879
OPPOSITION- WOODDELL et al., "Sustained liver‐specific transgene expression from the albumin promoter in mice following hydrodynamic plasmid DNA delivery", J Gene Med, (20080310), vol. 10, no. 5, doi:doi:10.1002/jgm.1179, pages 551 - 563, XP055041510
OPPOSITION- KELLENDONK et al., "Hepatocyte-Specific Expression of Cre Recombinase", Genesis, (20000200), vol. 26, no. 2, pages 151 - 153, XP055626886
OPPOSITION- NISHIMASU et al., "Crystal Structure of Cas9 in Complex Published 27 with Guide RNA and Target DNA", Cell, (20140213), vol. 156, no. 5, pages 935 - 949, XP028622533
OPPOSITION- SANDS et al., "Gene therapy for lysosomal storage diseases", Molecular Therapy, (20060500), vol. 13, no. 5, pages 839 - 849, XP005416300
OPPOSITION- ROSS et al., "Huntington's Disease: From Molecular Published Pathogenesis to Clinical Treatment", Lancet Neurol, (20110100), vol. 10, no. 1, pages 83 - 98, XP027599023
OPPOSITION- ESVELT et al., "Genome-scale engineering for systems and synthetic biology", Molecular Systems Biology, (20130100), vol. 9, pages 1 - 17, XP055339996
OPPOSITION- CARROLL D., "A CRISPR Approach to Gene Targeting", Molecular Therapy, (20120900), vol. 20, no. 9, pages 1658 - 1660, XP055106489
OPPOSITION- LI et al., "In vivo genome editing restores haemostasis in a mouse model of haemophilia", Nature, (20110714), vol. 475, no. 7355, pages 217 - 221, XP002688791
OPPOSITION- SADELAIN et al., "Safe harbours for the integration of new DNA in the human genome", Nature Reviews Cancer, (20120100), vol. 12, no. 1, pages 51 - 58, XP055018235
OPPOSITION- NGUYEN & FERRY, "Liver gene therapy: advances and hurdles", Gene Therapy, (20041000), vol. 11, no. S1, pages S76 - S84, XP055626878
OPPOSITION- JINEK et al., "A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity", Science, (20120817), vol. 337, no. 6096, pages 816 - 821, XP055067740
OPPOSITION- MALI et al., "RNA-Guided Human Genome Engineering Published 15 via Cas9", Science, (20130215), vol. 339, no. 6121, pages 823 - 826, XP055111247
OPPOSITION- MALI et al., "RNA-Guided Human Genome Engineering via Cas9", Science, (20130215), vol. 339, no. 6121, pages 823 - 826, XP055111247
OPPOSITION- RICHARD, "The genetic and molecular bases of monogenic disorders affecting proteolytic systems", J Med Genet, (20050700), vol. 42, no. 7, pages 529 - 539, XP055626421
OPPOSITION- FOLLENZI et al., "Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice", Blood, (20040515), vol. 103, no. 10, pages 3700 - 3709, XP055626883
OPPOSITION- PORTEUS et al., "A Look to Future Directions in Gene Therapy Research for Monogenic Diseases", PLoS Genetics, (20060100), vol. 2, no. 9, page e133, XP055626854
OPPOSITION- CARROLL, "Genome Engineering With Zinc-Finger Nucleases", Genetics, (20110800), vol. 188, no. 4, pages 773 - 782, XP055171682
OPPOSITION- PELLETIER et al., "RNA Based Gene Therapy for Dominantly Inherited Diseases", Current Gene Therapy, (20060200), vol. 6, no. 1, pages 131 - 146, XP055626873
OPPOSITION- SILVA et al., "Meganucleases and Other Tools for Targeted Genome Engineering: Perspectives and Challenges for Gene Therapy", Current Gene Therapy, (20110200), vol. 11, no. 1, pages 11 - 27, XP002706113
OPPOSITION- JINEK et al., "RNA-programmed genome editing in human cells", eLife 2, (20130129), vol. 2, page e00471, XP002699851
OPPOSITION- David J Segal, "Bacteria herald a new era of gene editing", eLife 2, (20130129), vol. 2, page e00563, XP055626867
SEARCH- Anguela et al., "In Vivo Genome Editing of Liver Albumin for Therapeutic Gene Expression: Rescue of Hemophilic Mice Via Integration of Factor 9", 54th ASH Annual Meeting and Exposition, Atlanta, USA, (20121210), Database accession no. 751, URL: https://ash.confex.com/ash/2012/webprogram/Paper51404.html, (20130926), XP002713765 [XP] 1-6,9,10 * abstract *
SEARCH- GRABOWSKI ET AL, "Phenotype, diagnosis, and treatment of Gaucher's disease", THE LANCET, LANCET LIMITED. LONDON, GB, vol. 372, no. 9645, doi:10.1016/S0140-6736(08)61522-6, ISSN 0140-6736, (20081004), pages 1263 - 1271, (20081002), XP025480739 [A] 1-6,8-14 * the whole document *
SEARCH- MONICA DAGNINO ET AL, "Molecular Diagnosis of Analbuminemia: A New Case Caused by a Nonsense Mutation in the Albumin Gene", INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, (20111225), vol. 12, no. 12, doi:10.3390/ijms12117314, ISSN 1661-6596, pages 7314 - 7322, XP055081308 [A] 1-6,8-14 * the whole document *

Download Citation Report

Get a free citation report including examiner, opposition, and international search citations.

Get Citation Report

Dossier Documents

The dossier documents provide a comprehensive record of the patent’s prosecution history - including filings, correspondence, and decisions made by patent offices - and are crucial for understanding the patent’s legal journey and any challenges it may have faced during examination.

  • Date

    Description

  • Get instant alerts for new documents